Topic
dravet-syndrome
1 stories related to this topic, newest first.
prnewswire.comhealth16 days agoDeveloping
Encoded Therapeutics Reports Initial Results from Gene Therapy Trial for Dravet Syndrome
A trial by Encoded Therapeutics involving 21 children with Dravet syndrome showed that sirolimus, used alongside steroids to prevent immune responses, could blunt the therapy's benefits. The findings, published May 13, 2026, come from a Boston-based report examining a key concern…