gene therapy
5 stories related to this topic, newest first.
Robert Hammer / Wikimedia (Public domain)Researchers Use Vectors to Deliver HIV Drug and Suppress Virus in Macaques for Up to One Year
A study demonstrated that adeno-associated vectors can deliver the CCR5-blocking HIV drug leronlimab. A single dose led to leronlimab expression and partial suppression of SHIV in infected macaques for as long as one year. The findings were reported in a scientific journal.
marketwatch.comRegeneron Agrees to Lower Drug Prices and Offer Free Gene Therapy in U.S. Deal
Biotech company Regeneron has entered into an agreement with the U.S. government to reduce medication costs for American patients. The deal includes offering a new hearing-loss gene therapy at no charge to eligible individuals. This is part of broader efforts to align U.S. drug p…
Substrate placeholder — needs review · Wikimedia Commons (CC BY-SA 3.0)Recent Advances in Gene Therapy for Rare Diseases Reported
Developments in gene therapy and targeted medications have shown progress in treating rare diseases such as spinal muscular atrophy and certain forms of blindness. These conditions affect an estimated 30 million people in the United States, with over 7,000 identified rare disease…
Substrate placeholder — needs review · Wikimedia Commons (CC BY-SA 3.0)Asia Summit on Global Health Scheduled for May 2026 in Hong Kong
The Asia Summit on Global Health (ASGH) 2026 will take place on May 11-12 in Hong Kong. The event will cover topics including gene and cell therapies, precision medicine, smart ageing, artificial intelligence, and digital health. Organizers invite participants to register for the…
Substrate placeholder — needs review · Wikimedia Commons (CC BY-SA 3.0)Elevidys Gene Therapy Shows Positive Results in Duchenne Muscular Dystrophy Trial
Sarepta Therapeutics reported positive topline results from a phase 3 trial of its gene therapy Elevidys for Duchenne muscular dystrophy. The trial met its primary endpoint of improved motor function in patients aged 4 to 7. The Duchenne muscular dystrophy field has experienced s…