Topic
hemoglobinopathy
1 stories related to this topic, newest first.
Mark Klimek / Wikimedia (CC BY-SA 2.0)science61 days ago
Clinical Trial Demonstrates Base Editing Effectiveness for β-Thalassaemia Treatment
Researchers have applied base editing to treat β-thalassaemia in a clinical setting, reactivating the fetal hemoglobin gene. The trial shows improved gene editing processes that address the blood disorder. This development builds on prior research in gene therapy for hemoglobinop…
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